Designation is supported by an exploratory analysis from the Phase 1b study showing that some children with SMA previously treated with gene ...

Biogen BIIB recently announced that the FDA has granted Breakthrough Therapy designation to Salanersen, an investigational ...

A lightweight robotic device has helped children with spinal muscular atrophy (SMA) achieve a ...

Spinal muscular atrophy (SMA) is a genetic neuromuscular disease affecting specialized nerve cells that control voluntary muscle movement, according to the Muscular Dystrophy Association (MDA). It can ...

Salanersen, which is designed for once-yearly dosing, is a potential successor to Biogen's blockbuster SMA drug Spinraza, which generated worldwide sales of nearly $1.55 billion last year and requires ...

Forbes contributors publish independent expert analyses and insights. Spinal muscular atrophy affects the nerves that control muscle movement, leading to progressive weakening. As a result, infants ...

"Managing pain in patients with SMA begins with the recognition that there are predictable etiologies leading to pain in SMA and investigating them during each medical visit is important to implement ...

Ancient bacteria that have evolved to become integral to our cells—converting nutrients from food into energy—may also contribute to neurologic disorders, such as spinal muscular atrophy (SMA) and ...

Visakhapatnam: Inspired by the humanitarian vision of IT and HRD Minister Nara Lokesh, Visakhapatnam Metropolitan Region ...

A local family has a personal stake in the donations that pour into St. Jude Children’s Research Hospital. Every month, the ...

Regina Trollmann, MD, of the Division of Pediatric Neurology, Department of Pediatrics, Friedrich-Alexander-University of Erlangen-Nürnberg, Erlangen, Germany, and colleagues, did a retrospective ...