One of the most devastating diseases finally has a treatment that can slow its progression and transform lives, tearful ...

Pivotal results from uniQure’s gene therapy for Huntington’s disease have brought new light to patients who have known only ...

After years of heartbreak, researchers have found an experimental treatment that can slow the progression of Huntington’s ...

As well as slowing disease progression by 75 percent at 36 months, the scientists found that neurofilament light protein (NfL)—a biomarker of neuronal damage—levels in spinal fluid were lower in ...

A woman whose mother, aunt and grandmother died from Huntington's disease has described a breakthrough in treating the ...

Researchers announce breakthrough results for AMT-130, the first disease-modifying treatment for Huntington's disease, with ...

However, in late September 2025, scientists successfully treated Huntington’s for the first time in a ground-breaking study.

UniQure's therapy, called AMT-130, reduced disease progression by 75% at 36 months in patients who received a high dose.

An experimental gene therapy slowed Huntington’s by up to 75 percent in a small clinical trial. While not a cure, it may give patients longer lives.

Last month, “historic positive results” from uniQure’s gene therapy snapped the Huntington’s community out of years of failure. As the biotech prepares to submit for FDA approval, BioSpace looks at ...

Scientists have slowed the progression of Huntington’s disease for the first time with a “groundbreaking” new treatment. Experts from University College London (UCL) said the finding could “change ...

Huntington’s disease (HD) is a condition that is hereditary and causes nerve cells in specific parts of the brain to slowly deteriorate and die. The disorder affects regions responsible for controlled ...